Argov, Zohar

Aceneuramic Acid Extended Release Administration Maintains Upper Limb Muscle Strength in a 48-week Study of Subjects with GNE Myopathy: Results from a Phase 2, Randomized, Controlled Study. [electronic resource] - Journal of neuromuscular diseases 03 2016 - 49-66 p. digital

Publication Type: Clinical Trial, Phase II; Journal Article; Multicenter Study; Randomized Controlled Trial; Research Support, Non-U.S. Gov't

2214-3599

10.3233/JND-159900 doi


Adolescent
Adult
Distal Myopathies--drug therapy
Double-Blind Method
Female
Humans
Male
Middle Aged
N-Acetylneuraminic Acid--administration & dosage
Outcome Assessment, Health Care
Young Adult