Bahal, Raman <br/><br/>
In vivo correction of anaemia in β-thalassemic mice by γPNA-mediated gene editing with nanoparticle delivery.  [electronic resource] 

 -  Nature communications  10 2016 
 - 13304 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>2041-1723 
<br/><br/><label>Standard No.: </label>10.1038/ncomms13304  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Cell Line<br/>DNA--administration & dosage<br/>Disease Models, Animal<br/>Gene Editing--methods<br/>Genetic Therapy--methods<br/>Hematopoietic Stem Cells--metabolism<br/>Hemoglobins--analysis<br/>Humans<br/>Injections, Intravenous<br/>Mice<br/>Mice, Transgenic<br/>Nanoparticles--administration & dosage<br/>Peptide Nucleic Acids--administration & dosage<br/>Proto-Oncogene Proteins c-kit--metabolism<br/>Stem Cell Factor--administration & dosage<br/>beta-Globins--genetics<br/>beta-Thalassemia--blood