TY  - GEN
AU  - Ng,Kwong-Man
AU  - Mok,Pamela Y
AU  - Butler,Amy W
AU  - Ho,Jenny C Y
AU  - Choi,Shing-Wan
AU  - Lee,Yee-Ki
AU  - Lai,Wing-Hon
AU  - Au,Ka-Wing
AU  - Lau,Yee-Man
AU  - Wong,Lai-Yung
AU  - Esteban,Miguel A
AU  - Siu,Chung-Wah
AU  - Sham,Pak C
AU  - Colman,Alan
AU  - Tse,Hung-Fat
TI  - Amelioration of X-Linked Related Autophagy Failure in Danon Disease With DNA Methylation Inhibitor
SN  - 1524-4539
PY  - 2017///0428
KW  - Adult
KW  - Alleles
KW  - Autophagy
KW  - drug effects
KW  - Azacitidine
KW  - pharmacology
KW  - Cell Line
KW  - Chromosomes, Human, X
KW  - genetics
KW  - Female
KW  - Glycogen Storage Disease Type IIb
KW  - Humans
KW  - Induced Pluripotent Stem Cells
KW  - metabolism
KW  - Lysosomal-Associated Membrane Protein 2
KW  - biosynthesis
KW  - Male
N1  - Publication Type: Case Reports; Journal Article
UR  - https://doi.org/10.1161/CIRCULATIONAHA.115.019847
ER  -