Ou, Zhanhui <br/><br/>
The Combination of CRISPR/Cas9 and iPSC Technologies in the Gene Therapy of Human β-thalassemia in Mice.  [electronic resource] 

 -  Scientific reports  09 2016 
 - 32463 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>2045-2322 
<br/><br/><label>Standard No.: </label>10.1038/srep32463  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>CRISPR-Cas Systems<br/>Cell Differentiation<br/>Female<br/>Gene Editing--methods<br/>Gene Expression<br/>Genetic Therapy--methods<br/>Hematopoietic Stem Cell Transplantation<br/>Hematopoietic Stem Cells--cytology<br/>Homologous Recombination<br/>Humans<br/>Induced Pluripotent Stem Cells--metabolism<br/>Interleukin Receptor Common gamma Subunit--deficiency<br/>Mice<br/>Mice, Inbred NOD<br/>Mice, SCID<br/>Mutation<br/>Whole-Body Irradiation<br/>beta-Globins--deficiency<br/>beta-Thalassemia--genetics