Odermatt, Philipp <br/><br/>
Somatic Therapy of a Mouse SMA Model with a U7 snRNA Gene Correcting SMN2 Splicing.  [electronic resource] 

 -  Molecular therapy : the journal of the American Society of Gene Therapy  10 2016 
 - 1797-1805 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1525-0024 
<br/><br/><label>Standard No.: </label>10.1038/mt.2016.152  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Adenoviridae--genetics<br/>Animals<br/>Disease Models, Animal<br/>Genetic Therapy--methods<br/>Genetic Vectors--administration & dosage<br/>Liver--metabolism<br/>Mice<br/>Mice, Transgenic<br/>Muscular Atrophy, Spinal--genetics<br/>Myocardium--metabolism<br/>RNA Splicing<br/>RNA, Small Nuclear--administration & dosage<br/>Survival of Motor Neuron 2 Protein--genetics