Restoration of R117H CFTR folding and function in human airway cells through combination treatment with VX-809 and VX-770. [electronic resource]
- American journal of physiology. Lung cellular and molecular physiology 09 2016
- L550-9 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1522-1504
10.1152/ajplung.00186.2016 doi
Aminophenols--pharmacology Aminopyridines--pharmacology Benzodioxoles--pharmacology Cell Line Cystic Fibrosis--drug therapy Cystic Fibrosis Transmembrane Conductance Regulator--genetics Drug Evaluation, Preclinical Humans Mutation, Missense Protein Folding--drug effects Quinolones--pharmacology Sequence Deletion