Gentzsch, Martina

Restoration of R117H CFTR folding and function in human airway cells through combination treatment with VX-809 and VX-770. [electronic resource] - American journal of physiology. Lung cellular and molecular physiology 09 2016 - L550-9 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1522-1504

10.1152/ajplung.00186.2016 doi


Aminophenols--pharmacology
Aminopyridines--pharmacology
Benzodioxoles--pharmacology
Cell Line
Cystic Fibrosis--drug therapy
Cystic Fibrosis Transmembrane Conductance Regulator--genetics
Drug Evaluation, Preclinical
Humans
Mutation, Missense
Protein Folding--drug effects
Quinolones--pharmacology
Sequence Deletion