Bashar, Abu E

An ex vivo gene therapy approach in X-linked retinoschisis. [electronic resource] - Molecular vision 2016 - 718-33 p. digital

Publication Type: Journal Article

1090-0535


Animals
Cytomegalovirus--genetics
Disease Models, Animal
Electroporation
Electroretinography
Enzyme-Linked Immunosorbent Assay
Eye Proteins--genetics
Female
Gene Expression Regulation--physiology
Gene Transfer Techniques
Genetic Therapy
Genetic Vectors
Humans
Intravitreal Injections
Male
Mesenchymal Stem Cells--metabolism
Mice
Mice, Inbred C57BL
Mice, Knockout
Real-Time Polymerase Chain Reaction
Retina--physiology
Retinoschisis--genetics
Transfection