Bashar, Abu E
An ex vivo gene therapy approach in X-linked retinoschisis. [electronic resource]
- Molecular vision 2016
- 718-33 p. digital
Publication Type: Journal Article
1090-0535
Animals
Cytomegalovirus--genetics
Disease Models, Animal
Electroporation
Electroretinography
Enzyme-Linked Immunosorbent Assay
Eye Proteins--genetics
Female
Gene Expression Regulation--physiology
Gene Transfer Techniques
Genetic Therapy
Genetic Vectors
Humans
Intravitreal Injections
Male
Mesenchymal Stem Cells--metabolism
Mice
Mice, Inbred C57BL
Mice, Knockout
Real-Time Polymerase Chain Reaction
Retina--physiology
Retinoschisis--genetics
Transfection