CRISPR Repair Reveals Causative Mutation in a Preclinical Model of Retinitis Pigmentosa. [electronic resource]
- Molecular therapy : the journal of the American Society of Gene Therapy Aug 2016
- 1388-94 p. digital
Publication Type: Journal Article
1525-0024
10.1038/mt.2016.107 doi
Animals CRISPR-Cas Systems Clustered Regularly Interspaced Short Palindromic Repeats Cyclic Nucleotide Phosphodiesterases, Type 6--genetics DNA Repair Disease Models, Animal Electroretinography Exons Gene Editing Genetic Loci Homologous Recombination Mice Mice, Transgenic Mutation Photoreceptor Cells, Vertebrate--metabolism RNA, Guide, CRISPR-Cas Systems Retinal Degeneration--genetics Retinitis Pigmentosa--genetics