Wu, Wen-Hsuan

CRISPR Repair Reveals Causative Mutation in a Preclinical Model of Retinitis Pigmentosa. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Aug 2016 - 1388-94 p. digital

Publication Type: Journal Article

1525-0024

10.1038/mt.2016.107 doi


Animals
CRISPR-Cas Systems
Clustered Regularly Interspaced Short Palindromic Repeats
Cyclic Nucleotide Phosphodiesterases, Type 6--genetics
DNA Repair
Disease Models, Animal
Electroretinography
Exons
Gene Editing
Genetic Loci
Homologous Recombination
Mice
Mice, Transgenic
Mutation
Photoreceptor Cells, Vertebrate--metabolism
RNA, Guide, CRISPR-Cas Systems
Retinal Degeneration--genetics
Retinitis Pigmentosa--genetics