TY  - GEN
AU  - Gao,Yuanzheng
AU  - Guo,Xiuming
AU  - Santostefano,Katherine
AU  - Wang,Yanlin
AU  - Reid,Tammy
AU  - Zeng,Desmond
AU  - Terada,Naohiro
AU  - Ashizawa,Tetsuo
AU  - Xia,Guangbin
TI  - Genome Therapy of Myotonic Dystrophy Type 1 iPS Cells for Development of Autologous Stem Cell Therapy
SN  - 1525-0024
PY  - 2017///0606
KW  - Animals
KW  - Cell Differentiation
KW  - Cell Nucleus
KW  - metabolism
KW  - Cell Transformation, Neoplastic
KW  - genetics
KW  - Disease Models, Animal
KW  - Gene Targeting
KW  - Genetic Loci
KW  - Genetic Therapy
KW  - Humans
KW  - Induced Pluripotent Stem Cells
KW  - cytology
KW  - Mice
KW  - Myocytes, Cardiac
KW  - Myotonic Dystrophy
KW  - Myotonin-Protein Kinase
KW  - Poly A
KW  - Protein Binding
KW  - RNA Splicing
KW  - Stem Cell Transplantation
KW  - Teratoma
KW  - Transcription Activator-Like Effector Nucleases
KW  - Transplantation, Autologous
KW  - Trinucleotide Repeats
N1  - Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, N.I.H., Extramural
UR  - https://doi.org/10.1038/mt.2016.97
ER  -