Lee, Stanley Chun-Wei
Modulation of splicing catalysis for therapeutic targeting of leukemia with mutations in genes encoding spliceosomal proteins. [electronic resource]
- Nature medicine 06 2016
- 672-8 p. digital
Publication Type: Journal Article
ISSN: 1546-170X
Standard No.: 10.1038/nm.4097 doi
Subjects--Topical Terms: Anemia, Aplastic--genetics Animals Bone Marrow Diseases--genetics Bone Marrow Failure Disorders Bone Marrow Transplantation Catalysis Cell Line, Tumor Epoxy Compounds--pharmacology Flow Cytometry Gene Knock-In Techniques Hemizygote Hemoglobinuria, Paroxysmal--genetics Humans Leukemia, Myeloid, Acute--genetics Macrolides--pharmacology Mice Mice, Knockout Mutation Myelodysplastic Syndromes--genetics Neoplasm Transplantation RNA Splicing--drug effects Reverse Transcriptase Polymerase Chain Reaction Serine-Arginine Splicing Factors--genetics Spliceosomes--genetics