Lee, Stanley Chun-Wei

Modulation of splicing catalysis for therapeutic targeting of leukemia with mutations in genes encoding spliceosomal proteins. [electronic resource] - Nature medicine 06 2016 - 672-8 p. digital

Publication Type: Journal Article

1546-170X

10.1038/nm.4097 doi


Anemia, Aplastic--genetics
Animals
Bone Marrow Diseases--genetics
Bone Marrow Failure Disorders
Bone Marrow Transplantation
Catalysis
Cell Line, Tumor
Epoxy Compounds--pharmacology
Flow Cytometry
Gene Knock-In Techniques
Hemizygote
Hemoglobinuria, Paroxysmal--genetics
Humans
Leukemia, Myeloid, Acute--genetics
Macrolides--pharmacology
Mice
Mice, Knockout
Mutation
Myelodysplastic Syndromes--genetics
Neoplasm Transplantation
RNA Splicing--drug effects
Reverse Transcriptase Polymerase Chain Reaction
Serine-Arginine Splicing Factors--genetics
Spliceosomes--genetics