Choudhury, Sourav R

In Vivo Selection Yields AAV-B1 Capsid for Central Nervous System and Muscle Gene Therapy. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy 08 2016 - 1247-57 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural

1525-0024

10.1038/mt.2016.84 doi


Animals
Capsid Proteins--chemistry
Central Nervous System--metabolism
Dependovirus--classification
Gene Expression
Gene Transfer Techniques
Genes, Reporter
Genetic Therapy
Genetic Vectors--administration & dosage
Humans
Mice
Models, Molecular
Muscles--metabolism
Protein Conformation
Transduction, Genetic
Transgenes
Viral Tropism