Wasala, Nalinda B

Genomic removal of a therapeutic mini-dystrophin gene from adult mice elicits a Duchenne muscular dystrophy-like phenotype. [electronic resource] - Human molecular genetics 07 2016 - 2633-2644 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, N.I.H., Extramural; Research Support, U.S. Gov't, Non-P.H.S.

1460-2083

10.1093/hmg/ddw123 doi


Animals
Dystrophin--genetics
Gene Expression
Gene Transfer Techniques
Genetic Therapy--methods
Genetic Vectors
Genomics
Mice
Mice, Inbred CBA
Mice, Inbred mdx
Mice, Transgenic
Muscle, Skeletal--metabolism
Muscular Dystrophy, Animal--genetics
Muscular Dystrophy, Duchenne--genetics
Myocardium--metabolism