TY  - GEN
AU  - Kakkis,Emil D
AU  - Kowalcyk,Sara
AU  - Bronstein,Max G
TI  - Accessing the accelerated approval pathway for rare disease therapeutics
SN  - 1546-1696
PY  - 2016///0823
KW  - Biomarkers
KW  - analysis
KW  - Drug Approval
KW  - legislation & jurisprudence
KW  - Humans
KW  - Rare Diseases
KW  - diagnosis
KW  - United States
KW  - United States Food and Drug Administration
N1  - Publication Type: Journal Article
UR  - https://doi.org/10.1038/nbt.3530
ER  -