Kakkis, Emil D <br/><br/>
Accessing the accelerated approval pathway for rare disease therapeutics.  [electronic resource] 

 -  Nature biotechnology  Apr 2016 
 - 380-3 p.  digital 
<br/><br/> Publication Type: Journal Article 
<br/><br/><label>ISSN: </label>1546-1696 
<br/><br/><label>Standard No.: </label>10.1038/nbt.3530  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Biomarkers--analysis<br/>Drug Approval--legislation & jurisprudence<br/>Humans<br/>Rare Diseases--diagnosis<br/>United States<br/>United States Food and Drug Administration