Vulin, Adeline

The first exon duplication mouse model of Duchenne muscular dystrophy: A tool for therapeutic development. [electronic resource] - Neuromuscular disorders : NMD Nov 2015 - 827-34 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1873-2364

10.1016/j.nmd.2015.08.005 doi


Animals
Body Weight
Creatine Kinase--metabolism
Disease Models, Animal
Exons
Gene Duplication
Gene Knock-In Techniques--methods
Male
Mice, Inbred mdx
Mice, Transgenic
Muscle, Skeletal--metabolism
Muscular Dystrophy, Duchenne--genetics
Phenotype
RNA, Messenger--metabolism