Pandey, Sanjay K <br/><br/>
Identification and characterization of modified antisense oligonucleotides targeting DMPK in mice and nonhuman primates for the treatment of myotonic dystrophy type 1.  [electronic resource] 

 -  The Journal of pharmacology and experimental therapeutics  Nov 2015 
 - 329-40 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, N.I.H., Extramural 
<br/><br/><label>ISSN: </label>1521-0103 
<br/><br/><label>Standard No.: </label>10.1124/jpet.115.226969  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Cell Line<br/>Humans<br/>Macaca fascicularis<br/>Male<br/>Mice<br/>Mice, Transgenic<br/>Muscle, Skeletal--enzymology<br/>Myotonic Dystrophy--drug therapy<br/>Myotonin-Protein Kinase--antagonists & inhibitors<br/>Oligonucleotides--chemistry<br/>Oligonucleotides, Antisense--pharmacology<br/>RNA, Messenger--metabolism<br/>Rats<br/>Rats, Sprague-Dawley