Yamamoto, H

BTK gene targeting by homologous recombination using a helper-dependent adenovirus/adeno-associated virus hybrid vector. [electronic resource] - Gene therapy Feb 2016 - 205-13 p. digital

Publication Type: Evaluation Study; Journal Article; Research Support, Non-U.S. Gov't

1476-5462

10.1038/gt.2015.91 doi


Agammaglobulinaemia Tyrosine Kinase
Agammaglobulinemia--genetics
Cell Line, Tumor
Dependovirus--genetics
Gene Targeting
Genetic Diseases, X-Linked--genetics
Genetic Therapy
Genetic Vectors--genetics
Helper Viruses--genetics
Homologous Recombination
Humans
Male
Mutation
Protein-Tyrosine Kinases--genetics