TDP-43 repression of nonconserved cryptic exons is compromised in ALS-FTD. [electronic resource]
- Science (New York, N.Y.) Aug 2015
- 650-5 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1095-9203
10.1126/science.aab0983 doi
Amyotrophic Lateral Sclerosis--genetics Animals Autophagy-Related Proteins Base Sequence Cells, Cultured Cysteine Endopeptidases--genetics DNA-Binding Proteins--genetics Embryonic Stem Cells Exons--genetics Frontotemporal Dementia--genetics Gene Knockout Techniques HeLa Cells Humans Mice Molecular Sequence Data Protein Isoforms--genetics RNA Splicing RNA Stability RNA, Messenger--metabolism Sequence Analysis, DNA