Sahashi, Kentaro

Silencing neuronal mutant androgen receptor in a mouse model of spinal and bulbar muscular atrophy. [electronic resource] - Human molecular genetics Nov 2015 - 5985-94 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1460-2083

10.1093/hmg/ddv300 doi


Animals
Disease Progression
Gene Expression--drug effects
Gene Silencing
Mice
Mice, Transgenic
Motor Neurons
Muscle, Skeletal--pathology
Muscular Atrophy, Spinal--genetics
Mutation
Neuromuscular Junction--pathology
Oligonucleotides, Antisense--administration & dosage
Receptors, Androgen--genetics