Lieberman, Judy
Harnessing RNA interference for therapy: the silent treatment. [electronic resource]
- JAMA
- 1207-8 p. digital
Publication Type: Journal Article
1538-3598
10.1001/jama.2015.1241 doi
Gene Knockdown Techniques
Genetic Therapy--methods
Hemophilia A--therapy
Humans
Liver--drug effects
RNA Interference
RNA, Small Interfering