Crane, Ana M

Targeted correction and restored function of the CFTR gene in cystic fibrosis induced pluripotent stem cells. [electronic resource] - Stem cell reports Apr 2015 - 569-77 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

2213-6711

10.1016/j.stemcr.2015.02.005 doi


Alleles
Cell Differentiation--genetics
Cell Line
Cells, Cultured
Cystic Fibrosis--genetics
Cystic Fibrosis Transmembrane Conductance Regulator--genetics
Endonucleases--genetics
Gene Expression
Gene Targeting--methods
Genetic Vectors--genetics
Genotype
Homologous Recombination
Humans
Induced Pluripotent Stem Cells--cytology
Mutation
Recombinational DNA Repair
Sequence Analysis, DNA
Zinc Fingers--genetics