Han, Zongchao

Genomic DNA nanoparticles rescue rhodopsin-associated retinitis pigmentosa phenotype. [electronic resource] - FASEB journal : official publication of the Federation of American Societies for Experimental Biology Jun 2015 - 2535-44 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1530-6860

10.1096/fj.15-270363 doi


Animals
Blotting, Western
DNA--administration & dosage
Disease Models, Animal
Gene Expression Regulation
Gene Transfer Techniques
Genetic Therapy--methods
Humans
Introns--genetics
Mice, Knockout
Microscopy, Confocal
Microscopy, Electron, Transmission
Nanoparticles
Phenotype
Reproducibility of Results
Retina--metabolism
Retinitis Pigmentosa--genetics
Reverse Transcriptase Polymerase Chain Reaction
Rhodopsin--deficiency