Mearini, Giulia Mybpc3 gene therapy for neonatal cardiomyopathy enables long-term disease prevention in mice. [electronic resource] - Nature communications Dec 2014 - 5515 p. digital Publication Type: Journal Article; Research Support, Non-U.S. Gov't ISSN: 2041-1723 Standard No.: 10.1038/ncomms6515 doi Subjects--Topical Terms: AnimalsCardiomyopathy, Hypertrophic, Familial--geneticsCarrier Proteins--geneticsDependovirusGene Knock-In TechniquesGenetic Therapy--methodsHomozygoteMiceRNA, Messenger--metabolism