Mearini, Giulia

Mybpc3 gene therapy for neonatal cardiomyopathy enables long-term disease prevention in mice. [electronic resource] - Nature communications Dec 2014 - 5515 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

2041-1723

10.1038/ncomms6515 doi


Animals
Cardiomyopathy, Hypertrophic, Familial--genetics
Carrier Proteins--genetics
Dependovirus
Gene Knock-In Techniques
Genetic Therapy--methods
Homozygote
Mice
RNA, Messenger--metabolism