Wraith, J E
Mucopolysaccharidosis type I. [electronic resource]
- Pediatric endocrinology reviews : PER Sep 2014
- 102-6 p. digital
Publication Type: Journal Article; Review
1565-4753
Combined Modality Therapy
Enzyme Replacement Therapy
Hematopoietic Stem Cell Transplantation
Humans
Iduronidase--therapeutic use
Mucopolysaccharidosis I--diagnosis
Treatment Outcome