Bahal, Raman

Single-stranded γPNAs for in vivo site-specific genome editing via Watson-Crick recognition. [electronic resource] - Current gene therapy 2014 - 331-42 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S.

1875-5631

10.2174/1566523214666140825154158 doi


Animals
Bone Marrow--metabolism
DNA--administration & dosage
Gene Targeting
Green Fluorescent Proteins--genetics
High-Throughput Nucleotide Sequencing
Humans
Lactic Acid
Mice
Mice, Transgenic
Nanoparticles--administration & dosage
Peptide Nucleic Acids--administration & dosage
Polyglycolic Acid
Polylactic Acid-Polyglycolic Acid Copolymer
RNA Editing
Tissue Donors
beta-Globins--genetics