Su, Zhaoming

Discovery of a biomarker and lead small molecules to target r(GGGGCC)-associated defects in c9FTD/ALS. [electronic resource] - Neuron Sep 2014 - 1043-50 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, N.I.H., Intramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S.

1097-4199

10.1016/j.neuron.2014.07.041 doi


Adult
Aged
Amyotrophic Lateral Sclerosis--cerebrospinal fluid
Animals
Biomarkers--analysis
C9orf72 Protein
Cell Differentiation--drug effects
Cells, Cultured
Chlorocebus aethiops
DNA Repeat Expansion--genetics
Female
Fibroblasts
G-Quadruplexes
Humans
Male
Middle Aged
Nerve Tissue Proteins--metabolism
Neurons--metabolism
Protein Binding
Proteins--chemistry
RNA, Small Interfering--genetics