Williams, David A

Curing genetic disease with gene therapy. [electronic resource] - Transactions of the American Clinical and Climatological Association 2014 - 122-8; discussion 128-9 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

0065-7778


Animals
Clinical Trials, Phase I as Topic
Clinical Trials, Phase II as Topic
Cooperative Behavior
Gene Transfer Techniques
Genetic Therapy--adverse effects
Genetic Vectors--adverse effects
Humans
International Cooperation
Treatment Outcome
X-Linked Combined Immunodeficiency Diseases--genetics