Curing genetic disease with gene therapy. [electronic resource]
- Transactions of the American Clinical and Climatological Association 2014
- 122-8; discussion 128-9 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
0065-7778
Animals Clinical Trials, Phase I as Topic Clinical Trials, Phase II as Topic Cooperative Behavior Gene Transfer Techniques Genetic Therapy--adverse effects Genetic Vectors--adverse effects Humans International Cooperation Treatment Outcome X-Linked Combined Immunodeficiency Diseases--genetics