TY  - GEN
AU  - van der Meijden,J C
AU  - Güngör,D
AU  - Kruijshaar,M E
AU  - Muir,A D J
AU  - Broekgaarden,H A
AU  - van der Ploeg,A T
TI  - Ten years of the international Pompe survey: patient reported outcomes as a reliable tool for studying treated and untreated children and adults with non-classic Pompe disease
SN  - 1573-2665
PY  - 2016///0325
KW  - Adolescent
KW  - Adult
KW  - Aged
KW  - Aged, 80 and over
KW  - Child
KW  - Child, Preschool
KW  - Cohort Studies
KW  - Enzyme Replacement Therapy
KW  - methods
KW  - Fatigue
KW  - Female
KW  - Glycogen Storage Disease Type II
KW  - drug therapy
KW  - Humans
KW  - Infant
KW  - Infant, Newborn
KW  - Male
KW  - Middle Aged
KW  - Patient Outcome Assessment
KW  - Patient Participation
KW  - Quality of Life
KW  - Self Report
KW  - Young Adult
KW  - alpha-Glucosidases
KW  - therapeutic use
N1  - Publication Type: Journal Article; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1007/s10545-014-9751-2
ER  -