TY  - GEN
AU  - Finkel,Richard S
AU  - McDermott,Michael P
AU  - Kaufmann,Petra
AU  - Darras,Basil T
AU  - Chung,Wendy K
AU  - Sproule,Douglas M
AU  - Kang,Peter B
AU  - Foley,A Reghan
AU  - Yang,Michelle L
AU  - Martens,William B
AU  - Oskoui,Maryam
AU  - Glanzman,Allan M
AU  - Flickinger,Jean
AU  - Montes,Jacqueline
AU  - Dunaway,Sally
AU  - O'Hagen,Jessica
AU  - Quigley,Janet
AU  - Riley,Susan
AU  - Benton,Maryjane
AU  - Ryan,Patricia A
AU  - Montgomery,Megan
AU  - Marra,Jonathan
AU  - Gooch,Clifton
AU  - De Vivo,Darryl C
TI  - Observational study of spinal muscular atrophy type I and implications for clinical trials
SN  - 1526-632X
PY  - 2014///1211
KW  - Cohort Studies
KW  - Female
KW  - Humans
KW  - Infant
KW  - Male
KW  - Research Design
KW  - Spinal Muscular Atrophies of Childhood
N1  - Publication Type: Journal Article; Multicenter Study; Observational Study; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S
UR  - https://doi.org/10.1212/WNL.0000000000000741
ER  -