TY  - GEN
AU  - Osman,Erkan Y
AU  - Miller,Madeline R
AU  - Robbins,Kate L
AU  - Lombardi,Abby M
AU  - Atkinson,Arleigh K
AU  - Brehm,Amanda J
AU  - Lorson,Christian L
TI  - Morpholino antisense oligonucleotides targeting intronic repressor Element1 improve phenotype in SMA mouse models
SN  - 1460-2083
PY  - 2015///0423
KW  - Animals
KW  - Disease Models, Animal
KW  - Genetic Therapy
KW  - methods
KW  - Humans
KW  - Introns
KW  - Mice
KW  - Morpholinos
KW  - administration & dosage
KW  - Muscular Atrophy, Spinal
KW  - genetics
KW  - Regulatory Sequences, Nucleic Acid
KW  - Survival Rate
KW  - Survival of Motor Neuron 2 Protein
KW  - Weight Gain
N1  - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1093/hmg/ddu198
ER  -