Widemann, Brigitte C

Phase II trial of pirfenidone in children and young adults with neurofibromatosis type 1 and progressive plexiform neurofibromas. [electronic resource] - Pediatric blood & cancer Sep 2014 - 1598-602 p. digital

Publication Type: Clinical Trial, Phase II; Journal Article; Multicenter Study; Research Support, N.I.H., Intramural; Research Support, U.S. Gov't, Non-P.H.S.; Research Support, U.S. Gov't, P.H.S.

1545-5017

10.1002/pbc.25041 doi


Adolescent
Adult
Antineoplastic Agents--therapeutic use
Child
Child, Preschool
Disease Progression
Female
Follow-Up Studies
Humans
Male
Neoplasm Staging
Neurofibroma, Plexiform--drug therapy
Neurofibromatosis 1--drug therapy
Prognosis
Pyridones--therapeutic use
Quality of Life
Survival Rate
Time Factors
Tumor Necrosis Factor-alpha--antagonists & inhibitors
Young Adult