Khwaja, Omar S

Safety, pharmacokinetics, and preliminary assessment of efficacy of mecasermin (recombinant human IGF-1) for the treatment of Rett syndrome. [electronic resource] - Proceedings of the National Academy of Sciences of the United States of America Mar 2014 - 4596-601 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1091-6490

10.1073/pnas.1311141111 doi


Child
Child, Preschool
Female
Humans
Insulin-Like Growth Factor I--adverse effects
Intercellular Signaling Peptides and Proteins--adverse effects
Recombinant Proteins--adverse effects
Rett Syndrome--drug therapy