Sirrs, S M
Outcomes of patients treated through the Canadian Fabry disease initiative. [electronic resource]
- Molecular genetics and metabolism Apr 2014
- 499-506 p. digital
Publication Type: Journal Article; Randomized Controlled Trial; Research Support, Non-U.S. Gov't
ISSN: 1096-7206
Standard No.: 10.1016/j.ymgme.2014.01.014 doi
Subjects--Topical Terms: Adult Aged Canada Cardiovascular Diseases--etiology Cohort Studies Endpoint Determination Enzyme Replacement Therapy Fabry Disease--complications Female Humans Isoenzymes--therapeutic use Kaplan-Meier Estimate Male Middle Aged Recombinant Proteins Risk Factors Treatment Outcome alpha-Galactosidase--therapeutic use