VPAC2 receptor agonist BAY 55-9837 increases SMN protein levels and moderates disease phenotype in severe spinal muscular atrophy mouse models. [electronic resource]
- Orphanet journal of rare diseases Jan 2014
- 4 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1750-1172
10.1186/1750-1172-9-4 doi
Animals Disease Models, Animal Mice Muscular Atrophy, Spinal--drug therapy Peptide Fragments--therapeutic use Receptors, Vasoactive Intestinal Peptide, Type II--agonists Survival of Motor Neuron 1 Protein--metabolism Vasoactive Intestinal Peptide--therapeutic use