Repurposing diflunisal for familial amyloid polyneuropathy: a randomized clinical trial. [electronic resource]
- JAMA Dec 2013
- 2658-67 p. digital
Publication Type: Journal Article; Multicenter Study; Randomized Controlled Trial; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.
1538-3598
10.1001/jama.2013.283815 doi
Aged Amyloid Neuropathies, Familial--drug therapy Anti-Inflammatory Agents, Non-Steroidal--therapeutic use Body Mass Index Diflunisal--therapeutic use Disease Progression Double-Blind Method Female Humans Male Middle Aged Quality of Life Survival Analysis Treatment Outcome