TY - GEN AU - Zanetta,Chiara AU - Nizzardo,Monica AU - Simone,Chiara AU - Monguzzi,Erika AU - Bresolin,Nereo AU - Comi,Giacomo P AU - Corti,Stefania TI - Molecular therapeutic strategies for spinal muscular atrophies: current and future clinical trials SN - 1879-114X PY - 2014///1104 KW - Clinical Trials as Topic KW - Genetic Therapy KW - Humans KW - Molecular Targeted Therapy KW - Muscular Atrophy, Spinal KW - drug therapy KW - Survival of Motor Neuron 1 Protein KW - genetics KW - Survival of Motor Neuron 2 Protein N1 - Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Review; Systematic Review UR - https://doi.org/10.1016/j.clinthera.2013.11.006 ER -