Guo, Shuling Antisense oligonucleotide treatment ameliorates alpha-1 antitrypsin-related liver disease in mice. [electronic resource] - The Journal of clinical investigation Jan 2014 - 251-61 p. digital Publication Type: Journal Article ISSN: 1558-8238 Standard No.: 10.1172/JCI67968 doi Subjects--Topical Terms: AnimalsFemaleGene Knockdown TechniquesHep G2 CellsHepatocytes--enzymologyHumansLiver--enzymologyLiver Cirrhosis--enzymologyMacaca fascicularisMaleMiceMice, TransgenicOligonucleotides, Antisense--geneticsRNA, Messenger--geneticsalpha 1-Antitrypsin--geneticsalpha 1-Antitrypsin Deficiency--enzymology