Finkel, Richard S <br/><br/>
Phase 2a study of ataluren-mediated dystrophin production in patients with nonsense mutation Duchenne muscular dystrophy.  [electronic resource] 

 -  PloS one  2013 
 - e81302 p.  digital 
<br/><br/> Publication Type: Clinical Trial, Phase II; Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S. 
<br/><br/><label>ISSN: </label>1932-6203 
<br/><br/><label>Standard No.: </label>10.1371/journal.pone.0081302  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Child<br/>Codon, Nonsense--genetics<br/>Dystrophin--metabolism<br/>Humans<br/>Male<br/>Muscular Dystrophy, Duchenne--drug therapy<br/>Oxadiazoles--therapeutic use