Aiba, Yuichiro

Allele-selective inhibition of expression of huntingtin and ataxin-3 by RNA duplexes containing unlocked nucleic acid substitutions. [electronic resource] - Biochemistry Dec 2013 - 9329-38 p. digital

Publication Type: Comparative Study; Journal Article; Research Support, Non-U.S. Gov't

1520-4995

10.1021/bi4014209 doi


Alleles
Argonaute Proteins--metabolism
Ataxin-3
Base Pair Mismatch
Base Pairing
Base Sequence
Cell Line
Drug Design
Gene Silencing
Humans
Huntingtin Protein
Hydrolysis
Immunoprecipitation
Kinetics
Mutant Proteins--antagonists & inhibitors
Nerve Tissue Proteins--antagonists & inhibitors
Nuclear Proteins--antagonists & inhibitors
Oligonucleotides--chemistry
RNA, Messenger--antagonists & inhibitors
RNA, Small Interfering--chemistry
Recombinant Proteins--biosynthesis
Repressor Proteins--antagonists & inhibitors
Trinucleotide Repeats