Allele-selective inhibition of expression of huntingtin and ataxin-3 by RNA duplexes containing unlocked nucleic acid substitutions. [electronic resource]
- Biochemistry Dec 2013
- 9329-38 p. digital
Publication Type: Comparative Study; Journal Article; Research Support, Non-U.S. Gov't
1520-4995
10.1021/bi4014209 doi
Alleles Argonaute Proteins--metabolism Ataxin-3 Base Pair Mismatch Base Pairing Base Sequence Cell Line Drug Design Gene Silencing Humans Huntingtin Protein Hydrolysis Immunoprecipitation Kinetics Mutant Proteins--antagonists & inhibitors Nerve Tissue Proteins--antagonists & inhibitors Nuclear Proteins--antagonists & inhibitors Oligonucleotides--chemistry RNA, Messenger--antagonists & inhibitors RNA, Small Interfering--chemistry Recombinant Proteins--biosynthesis Repressor Proteins--antagonists & inhibitors Trinucleotide Repeats