Jameson, Elisabeth

Enzyme replacement therapy with laronidase (Aldurazyme) for treating mucopolysaccharidosis type I. [electronic resource] - The Cochrane database of systematic reviews Sep 2013 - CD009354 p. digital

Publication Type: Journal Article; Review; Systematic Review

1469-493X

10.1002/14651858.CD009354.pub2 doi


Enzyme Replacement Therapy--methods
Humans
Iduronidase--administration & dosage
Mucopolysaccharidosis I--classification
Randomized Controlled Trials as Topic
Rare Diseases--classification