Barbier, A J

The relationship between anti-idursulfase antibody status and safety and efficacy outcomes in attenuated mucopolysaccharidosis II patients aged 5 years and older treated with intravenous idursulfase. [electronic resource] - Molecular genetics and metabolism Nov 2013 - 303-10 p. digital

Publication Type: Clinical Trial, Phase II; Clinical Trial, Phase III; Journal Article

1096-7206

10.1016/j.ymgme.2013.08.002 doi


Administration, Intravenous
Adolescent
Adult
Antibodies--immunology
Child
Child, Preschool
Enzyme Replacement Therapy--adverse effects
Genotype
Glycoproteins--genetics
Glycosaminoglycans--urine
Humans
Iduronate Sulfatase--administration & dosage
Liver--metabolism
Mucopolysaccharidosis II--drug therapy
Organ Size
Spleen--metabolism
Treatment Outcome
Young Adult