Griesenbach, Uta
Moving forward: cystic fibrosis gene therapy. [electronic resource]
- Human molecular genetics Oct 2013
- R52-8 p. digital
Publication Type: Journal Article; Review
1460-2083
10.1093/hmg/ddt372 doi
Animals
Clinical Trials, Phase I as Topic
Clinical Trials, Phase II as Topic
Cystic Fibrosis--genetics
Cystic Fibrosis Transmembrane Conductance Regulator--genetics
Gene Transfer Techniques
Genetic Therapy--methods
Genetic Vectors
Humans
Lentivirus--genetics
Lung--pathology
Mice