Aoki, Yoshitsugu

Highly efficient in vivo delivery of PMO into regenerating myotubes and rescue in laminin-α2 chain-null congenital muscular dystrophy mice. [electronic resource] - Human molecular genetics Dec 2013 - 4914-28 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1460-2083

10.1093/hmg/ddt341 doi


Alternative Splicing
Animals
Base Sequence
Bromodeoxyuridine--metabolism
Cardiotoxins--administration & dosage
Cell Line
Cell Membrane Permeability--genetics
Disease Models, Animal
Dystrophin--chemistry
Exons
Gene Expression
Gene Order
Humans
Laminin--genetics
Mice
Mice, Knockout
Morpholinos--administration & dosage
Muscle Fibers, Skeletal--classification
Muscular Dystrophies--genetics
Muscular Dystrophy, Animal
Muscular Dystrophy, Duchenne--genetics
Regeneration