Beck, Michael

Natural history of alpha mannosidosis a longitudinal study. [electronic resource] - Orphanet journal of rare diseases Jun 2013 - 88 p. digital

Publication Type: Clinical Trial; Journal Article; Multicenter Study; Observational Study; Research Support, Non-U.S. Gov't

1750-1172

10.1186/1750-1172-8-88 doi


Adolescent
Adult
Child
Child, Preschool
Disease Progression
Female
Humans
Infant
Longitudinal Studies
Male
Physical Endurance
Respiratory Function Tests
Sulfatases--blood
Walking
Young Adult
alpha-Mannosidosis--physiopathology