TY  - GEN
AU  - Laraway,Sarah
AU  - Breen,Catherine
AU  - Mercer,Jean
AU  - Jones,Simon
AU  - Wraith,James E
TI  - Does early use of enzyme replacement therapy alter the natural history of mucopolysaccharidosis I? Experience in three siblings
SN  - 1096-7206
PY  - 2014///0122
KW  - Child
KW  - Child, Preschool
KW  - Enzyme Replacement Therapy
KW  - Female
KW  - Humans
KW  - Iduronidase
KW  - therapeutic use
KW  - Infant
KW  - Mucopolysaccharidosis I
KW  - drug therapy
KW  - Phenotype
KW  - Siblings
KW  - Treatment Outcome
N1  - Publication Type: Case Reports; Journal Article
UR  - https://doi.org/10.1016/j.ymgme.2013.04.023
ER  -