Laraway, Sarah <br/><br/>
Does early use of enzyme replacement therapy alter the natural history of mucopolysaccharidosis I? Experience in three siblings.  [electronic resource] 

 -  Molecular genetics and metabolism  Jul 2013 
 - 315-6 p.  digital 
<br/><br/> Publication Type: Case Reports; Journal Article 
<br/><br/><label>ISSN: </label>1096-7206 
<br/><br/><label>Standard No.: </label>10.1016/j.ymgme.2013.04.023  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Child<br/>Child, Preschool<br/>Enzyme Replacement Therapy<br/>Female<br/>Humans<br/>Iduronidase--therapeutic use<br/>Infant<br/>Mucopolysaccharidosis I--drug therapy<br/>Phenotype<br/>Siblings<br/>Treatment Outcome