Gedicke-Hornung, Christina <br/><br/>
Rescue of cardiomyopathy through U7snRNA-mediated exon skipping in Mybpc3-targeted knock-in mice.  [electronic resource] 

 -  EMBO molecular medicine  Jul 2013 
 - 1128-45 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1757-4684 
<br/><br/><label>Standard No.: </label>10.1002/emmm.201202168  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Adenoviridae--genetics<br/>Alternative Splicing<br/>Animals<br/>Cardiomyopathy, Hypertrophic--genetics<br/>Carrier Proteins--genetics<br/>Exons<br/>Gene Knock-In Techniques<br/>Genetic Therapy<br/>HEK293 Cells<br/>Heart--physiopathology<br/>Humans<br/>Hypertrophy, Left Ventricular--prevention & control<br/>Mice<br/>Mutation<br/>Myocardium--metabolism<br/>Oligoribonucleotides, Antisense--administration & dosage<br/>Protein Isoforms--genetics<br/>RNA, Messenger--genetics<br/>RNA, Small Nuclear--administration & dosage<br/>Transduction, Genetic