Gene therapy for misfolding protein diseases of the central nervous system. [electronic resource]
- Neurotherapeutics : the journal of the American Society for Experimental NeuroTherapeutics Jul 2013
- 498-510 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Review
1878-7479
10.1007/s13311-013-0191-8 doi
Animals Central Nervous System Diseases--complications Genetic Therapy--methods Humans Proteostasis Deficiencies--complications