San Sebastian, Waldy

Gene therapy for misfolding protein diseases of the central nervous system. [electronic resource] - Neurotherapeutics : the journal of the American Society for Experimental NeuroTherapeutics Jul 2013 - 498-510 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Review

1878-7479

10.1007/s13311-013-0191-8 doi


Animals
Central Nervous System Diseases--complications
Genetic Therapy--methods
Humans
Proteostasis Deficiencies--complications