Davies, Jane C Efficacy and safety of ivacaftor in patients aged 6 to 11 years with cystic fibrosis with a G551D mutation. [electronic resource] - American journal of respiratory and critical care medicine Jun 2013 - 1219-25 p. digital Publication Type: Journal Article; Multicenter Study; Randomized Controlled Trial; Research Support, Non-U.S. Gov't ISSN: 1535-4970 Standard No.: 10.1164/rccm.201301-0153OC doi Subjects--Topical Terms: Administration, OralAllelesAminophenols--administration & dosageChildCystic Fibrosis--drug therapyCystic Fibrosis Transmembrane Conductance Regulator--geneticsDNA--geneticsDose-Response Relationship, DrugDouble-Blind MethodForced Expiratory VolumeHumansLung--physiopathologyMutationQuinolones--administration & dosageRespiratory Function TestsTreatment Outcome