TY  - GEN
AU  - McIntosh,Jenny
AU  - Lenting,Peter J
AU  - Rosales,Cecilia
AU  - Lee,Doyoung
AU  - Rabbanian,Samira
AU  - Raj,Deepak
AU  - Patel,Nishil
AU  - Tuddenham,Edward G D
AU  - Christophe,Olivier D
AU  - McVey,John H
AU  - Waddington,Simon
AU  - Nienhuis,Arthur W
AU  - Gray,John T
AU  - Fagone,Paolo
AU  - Mingozzi,Federico
AU  - Zhou,Shang-Zhen
AU  - High,Katherine A
AU  - Cancio,Maria
AU  - Ng,Catherine Y C
AU  - Zhou,Junfang
AU  - Morton,Christopher L
AU  - Davidoff,Andrew M
AU  - Nathwani,Amit C
TI  - Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant
SN  - 1528-0020
PY  - 2013///0627
KW  - Animals
KW  - Blotting, Western
KW  - Dependovirus
KW  - genetics
KW  - Factor VIII
KW  - Genetic Therapy
KW  - Genetic Variation
KW  - Genetic Vectors
KW  - administration & dosage
KW  - Glycosylation
KW  - Hemophilia A
KW  - Humans
KW  - Immune Tolerance
KW  - Liver
KW  - metabolism
KW  - Macaca mulatta
KW  - Male
KW  - Mice
KW  - Mice, Inbred C57BL
KW  - Mice, Knockout
KW  - Peptide Fragments
KW  - Promoter Regions, Genetic
N1  - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1182/blood-2012-10-462200
ER  -